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# Draft Guide on Sanfilippo Syndrome Drugs
- URL: https://www.fdaweb.com/draft-guide-on-sanfilippo-syndrome-drugs/
- Published: 2020-02-05T12:00:00.000Z
- Updated: 2026-09-14T16:01:56.000Z
- Author: David McFarland
- Tags: Drugs, #legacy-id-D5146017

*Federal Register* notice: FDA has made available a draft guidance entitled “Mucopolysaccharidosis Type III (Sanfilippo Syndrome): Developing Drugs for Treatment.” The document is intended to enhance clinical trial data quality and support development of such treatments. It covers eligibility criteria, trial design considerations, and efficacy endpoints for use in clinical development programs. To view the notice, click [here](https://www.govinfo.gov/content/pkg/FR-2020-02-05/pdf/2020-02220.pdf?ref=fdaweb.com).