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# Rare Disease Endpoint Advancement Pilot
- URL: https://www.fdaweb.com/rare-disease-endpoint-advancement-pilot/
- Published: 2022-02-15T12:00:00.000Z
- Updated: 2026-09-14T17:32:47.000Z
- Author: David McFarland
- Tags: Drugs, #legacy-id-D5151163

A pilot program that could improve drug development and approval for rare diseases is part of the performance goals outlined for the upcoming PDUFA reauthorization. Medill News Service [reports](https://www.marketwatch.com/story/new-fda-program-could-boost-drug-development-for-rare-diseases-11644935201?mod=medill-news-service&ref=fdaweb.com) the pilot would be expected to bolster clinical trials for rare diseases by increasing collaboration between industry and the agency to determine meaningful endpoints for rare diseases in clinical trials.

The article also takes a broader look at the PDUFA program and some of its performance goals through the years.